what aspects of huntinton's disease pose challanges for designing a gene therapy? and why?
Gene Therapy What is gene therapy? what is it used for? is it effective? is it safe? What are the benefits? what are the challenges?
1.) What is gene therapy/gene intervention? What are the problems with gene therapy? In which tissues can gene therapy correct genetic defects, be inherited? 2.)What is the respect-for-persons priciple?
Describe what gene and stem therapy are used for, and why there is an ethical dilemma to use each in a person
1. Gene therapy involves inserting a functional copy of a gene into the genome to treat or prevent disease. However, in reality this process is not as easy as it sounds. What were some challenges the researchers faced as they tried to develop a gene therapy to treat Leber Congenital Amaurosis (LCA)? 2. Luxturna gene therapy officially costs $425,000 per eye ($850,000 for both eyes). Do you think that this is an appropriate price for this treatment?
2. Summarize the key aspects of each of the play therapy techniques. What do they involve and why might they be helpful for children?
Even though sickle-cell anemia is usually fatal to homozygous individuals, the disease persists because: Gene therapy has alleviated the condition The disease is carried on the dominant allele Individuals with one allele for sickle-cell anemia are resistant to malaria None of the above
Gene therapy is not necessarily a new technology, but it is technology that may finally make a contribution to human health. Create an initial post to this discussion where you argue both for and against the promotion of gene therapy as a viable option to treat genetic disease.
Prior to gene therapy with the agile allele (A), a male rat was homozygous (aa) for the autosomal recessive trait, awkwardness. Following the completion of the gene therapy, this same rat was test- crossed with a female rat of the appropriate genotype. What genotype should the female rat have in order for her to be used in a testcross? The offspring produced in the testcross were as follows: Assuming that the lest cross was performed correctly, what type of gene...
What is Harris's attitude toward gene therapy?
. If an adenoviral vector is used for gene therapy, why might it be necessary to give the patient multiple rounds? 4. How can a “suicide gene” be used to treat cancer? 5. Rexin-G is an effective vector for tumor treatment. Describe its 2 primary modes of action.